Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

Folder Abstracts

Documents

Toggle Title Date
pdf Poster Futerman ( pdf, 180 KB ) (3249 downloads) Popular
pdf Layman progress report Jiang(Aug 2019 Jan 2020) ( pdf, 162 KB ) (3054 downloads) Popular
pdf NTSAD2021 summary d'Azzo ( pdf, 110 KB ) (3083 downloads) Popular
pdf Sanofi Genzyme GM2 Patient Journey Poster ( pdf, 289 KB ) (3335 downloads) Popular
pdf 2019 September NTSAD d'Azzo Lay Summary 2019 ( pdf, 27 KB ) (2572 downloads) Popular
pdf 2019 September Gray Edwards NTSAD Lay Summary 0919 ( pdf, 109 KB ) (2833 downloads) Popular
pdf 2019 September Lay Progress Report Xuntian Jiang 12 months ( pdf, 164 KB ) (2720 downloads) Popular
pdf RT001 to Treat Neurodegeneration - Poster Presentation AAN 5 19 ( pdf, 92 KB ) (2904 downloads) Popular
pdf Natural History of LOTS - LDN-Eichler - Feb 2012 ( pdf, 630 KB ) (5052 downloads) Popular
pdf Poster Session DP2 Gangliosides ( pdf, 63 KB ) (5104 downloads) Popular
pdf Poster Session PSM06 Metabolism ( pdf, 344 KB ) (5720 downloads) Popular
pdf ABSTRACT NextGen Sequencing HEXA ( pdf, 253 KB ) (4550 downloads) Popular

Login